ʻO kaʻoihana o ka hoʻomohalaʻana a me ke kūʻaiʻana i nā lāʻau lapaʻau, heʻoihana nui loa ia, me nā hui e lawe mai i nā piliona kālā i kēlā me kēia makahiki. I ka Honua, kūʻaiʻia ke kūʻaiʻana i nā lāʻau lapaʻau i $ 1.3 miliona i ka 2018. He nui aku kaʻoihana kūʻai Pharma ma mua o ka huahana nui o nā'āina he 15, hui pūʻia. No kekahi poʻe,ʻo ka poʻe i loaʻa i nā maʻi maʻamau, hiki ke ukuʻia ka uku o kēia mau ola. ʻO nā lāʻau lapaʻauʻona, nā lāʻau i hoʻohanaʻia e mālama i nā maʻi iʻikeʻia e ka poʻeʻuʻuku wale nō, hiki ke uku pono i nā heluʻeono.
ʻO kekahi mau lālā ninaninauʻaʻole lākou e uhi i ka hapa nui a pau o kēia mau lāʻau lapaʻau, me ka waihoʻana i nāʻohana a me nā mea i hoʻopilikiaʻia e mālama i nā kumukūʻai iā lākou iho. He kaumaha nui kēia kālā no nā mea he nui a ua nui ka nānāʻana i kaʻoihana.
Ua hoʻokumuʻia kekahi mau mea i mea e hōʻoki ai i nā kumukūʻai, e like me nā hui'enelaʻole a me nā polokalamu kōkua kōkua. ʻOiai e hiki ke kōkua i kēia mau mea, he nui ka nui o nā kānaka i hikiʻole ke uku a me ka ukuʻana mai loko mai o ka waihona no kēia mau ola ola ola.
01 Glybera
ʻO kāna mea hana, UniQure, i'ōleloʻia ma ka 2017,ʻaʻole ia he mea e hōʻano hou ana i kaʻaeʻana i ka lāʻau lapaʻau ma Europa. ʻOiai ke kumu kūʻai nui,ʻaʻole loaʻaʻo Glybera ma muli o ke koiʻana o ka maʻi maʻi.
02 Soliris
Hiki i nā Soliris ke kūʻai i nā maʻi a hiki i $ 700,000 ma ka makahiki, kahi lāʻau maikaʻi i hoʻohanaʻia no ka mālamaʻana i ka hemoglobinuria nocturnal nocturnal. Aia 8,000 mau kānaka ma ka honua wale nō keʻano. Hoʻopau ka maʻi i nā kiʻekiʻenaʻulaʻula, e hana ana i nā maʻi i nā maʻi, anemia, a me nā kikoo koko.
I ka mahina o Kepakemapa 2017, ua kauoha nā luna o Kanada i ka mea hana Alexion Pharmaceuticals e hoʻohaʻahaʻa i ke kumukūʻai o Soliris, e kapa ana iā ia he keu.
03 Elaprase
Hoʻohanaʻia ka'ahuola e mālama ai i Hunter Syndrome, he kūlana koʻikoʻi e pili ana i nā kānaka he 500 wale nō maʻAmelika Huipūʻia nāna i pale i ka hana lolo a me ka hoʻolālā kino. ʻO ka uku makahiki no ka lāʻau lapaʻau ma luna o $ 500,000.
04 Naglazyme
Hanaʻiaʻo Naglazyme e mālama i ka Maroteaux-Lamy Syndrome, kahi kūlana e pili ana i nā mea pili. ʻO nā hōʻailona maʻamauʻo keʻano o ka hanaʻole, kāohi i ka uluʻana, nā pilikia o ka naʻau a me ka pohō o ka lolo. ʻO nā kumu lāʻau lapaʻau ma luna o $ 365,000.
05 Cinryze
Hoʻohanaʻo Cinryze i kahiʻano i kapaʻia he angioedema, kahi maʻi e pili ana i kahi 50,000 mau kānaka maʻAmelika Hui PūʻIa. Ma ke kumu kūʻai o $ 350,000 ma ka makahiki, hiki i ka lāʻau lāʻau ke hoʻoulu i ka'ōpiopio o nā lima, ka puʻu, a me ka'ōpū.
06 Folotyn
ʻO Folotyn kahi lāʻau lapaʻau no kahi maʻi kanikau i kapaʻia he lymphoma T-cell. Ua manaʻoʻia he hopena hope loa i hala noʻeono mau pule. Ma ke kumukūʻai o $ 320,000,ʻaʻole i hōʻikeʻia e hoʻolōʻihi i ke ola no ka lōʻihi loa, no laila ke hoʻohana mauʻia nei ma nāʻano koʻikoʻi wale nō.
07 O Acthar
Ua kauohaʻiaʻo Acthar e mālama i nā'ōpala a me ka hopuʻana. ʻO kēiaʻano e pili ana i nā keiki ma waena o nā makahikiʻehā me 11 mahina, akā ua'āponoʻiaʻo Acthar e mālama i nā keiki a hiki iʻelua makahiki. Hoʻohanaʻia nō hoʻi e mālama i nāʻano likeʻole o nā mākua, e like me ka maha o nā maʻi sclerosis. Kū'ē i ka $ 200,000 ma ka makahiki.
Ua noiʻia ka noi 2017 ma ka Journal of the American Medical Associaon i ka pono o Acthar, e hōʻike anaʻaʻole ia iʻoi aʻe ka maikaʻi ma mua o nā lawelaweʻana o nā lawelawe maʻamauʻole.
08 Myozyme
ʻO ka Myozyme he lāʻau lapaʻau no Pompe, he maʻi'eleʻaleʻa a ma kekahi mau maʻiʻeha e hōʻeha i ka naʻau a me nā olonāʻeleʻele. Ke hoʻopilikiaʻia nā kamaliʻi, make pinepine ka make i ka makahiki mua. ʻO koʻu myzyme he enzyme lysosomal glycogen-specific a ma nā haʻawina i hoʻonui i ka liʻiliʻi a me nā mea liʻiliʻi i kauʻia ma luna o nā mea hoʻolālā. ʻO ka uku makahiki ma waena o $ 100,000 a $ 300,000 i ka makahiki. ʻAʻole hiki ke loaʻa i kēia manawa i ka US